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  4. PAR-25-327

Translational Efforts to Advance Gene-based Therapies for Ultra-Rare Neurological and Neuromuscular Disorders (U01 - Clinical Trial Optional)

Deadline
2026-10-09
36 days left
Award ceiling
Awards
Posted
2024-12-18

Summary

The Ultra-Rare Gene-Based Therapy (URGenT) network supports Investigational New Drug (IND)-enabling studies and planning activities for First-in-Human (FIH) clinical testing of gene-based or transcript-directed therapeutics, such as oligonucleotides and viral-based gene therapies, for ultra-rare neurological or neuromuscular disorders. […]

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Official announcement: https://grants.nih.gov/grants/guide/pa-files/PAR-25-327.htmlSource: nih_guide+grants_gov. Always confirm dates with the funder.